Protein glycosylation was impaired and cell membrane exposure decreased in macrophages in vivo. selleck Single housing of homozygous C213G tissue factor males reduced the occurrence of severe bleeding and significantly improved survival, suggesting that inter-male aggressiveness might significantly account for the sex differences. These…[Read more]

In this review, we describe the most recent results from clinical trials. While ERT and gene therapy are the most developed therapies for MPS III, we highlight the work that needs to be done to bring us closer to a real treatment for these devastating diseases.

During the course of fellowship training, pediatric critical care fellows are…[Read more]

In this review, we describe the most recent results from clinical trials. While ERT and gene therapy are the most developed therapies for MPS III, we highlight the work that needs to be done to bring us closer to a real treatment for these devastating diseases.

During the course of fellowship training, pediatric critical care fellows are…[Read more]